SOURCE: Xtalks

Xtalks Webinars

July 18, 2017 07:30 ET

Into the Great Wide Open: PTC's transformation & Global Journey to Bring Patients a First Ever Rare Disease Therapy, New Webinar Hosted by Xtalks

TORONTO, ON--(Marketwired - July 18, 2017) - The rare disease biopharmaceutical landscape continues to evolve, but despite the advances made, only five percent of an estimated 7,000 rare diseases have an available treatment option. As life sciences companies begin to address the significant unmet need in the rare disease space, clinical-stage companies developing treatments for rare diseases face a number of challenges as they aim to bring products to market, particularly when on the global scale.

This webinar will explore PTC's journey from an R&D-only focus to a fully integrated, global commercial company as they launched Translarna™ the first disease-modifying treatment for Duchenne Muscular Dystrophy in the European market. The speakers will discuss the challenges of entering a new disease area for the first time, the balance of achieving the right size global organization to meet the customer population and the considerations for proceeding independently with a global launch rather than partnering.

Join the live broadcast on Monday, July 31, 2017 at 11am EDT (4pm BST/UK), featuring guest speakers Mark Rothera, Chief Commercial Officer at PTC Therapeutics, and Ned Kitfield, Vice President at Charles River Associates.

For more information or to register for this complimentary event visit: Into the Great Wide Open: PTC's transformation & Global Journey to Bring Patients a First Ever Rare Disease Therapy

Xtalks, powered by Honeycomb Worldwide Inc., is a leading provider of educational webinars to the global Life Sciences community. Every year thousands of industry practitioners (from pharmaceutical & biotech companies, private & academic research institutions, healthcare centers, etc.) turn to Xtalks for access to quality content. Xtalks helps Life Science professionals stay current with industry developments, trends and regulations. Xtalks webinars also provide perspectives on key issues from top industry thought leaders and service providers.

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